Muscle Gene Therapy

Muscle disease represents an important health threat to the general population. For thousands of years, a cure has been deemed extremely remote, if not impossible, for many relentless muscle diseases such as Duchenne muscular dystrophy. The cloning of muscle disease genes and the prospect of introdu...

Πλήρης περιγραφή

Λεπτομέρειες βιβλιογραφικής εγγραφής
Συγγραφή απο Οργανισμό/Αρχή: SpringerLink (Online service)
Άλλοι συγγραφείς: Duan, Dongsheng (Επιμελητής έκδοσης)
Μορφή: Ηλεκτρονική πηγή Ηλ. βιβλίο
Γλώσσα:English
Έκδοση: New York, NY : Springer New York, 2010.
Θέματα:
Διαθέσιμο Online:Full Text via HEAL-Link
Πίνακας περιεχομένων:
  • Animal Models for Inherited Muscle Diseases
  • In Utero Muscle Gene Transfer
  • Gene Therapy for the Respiratory Muscles
  • Muscular Dystrophy Gene Therapy in Small Animal Models
  • Antisense-Mediated Exon Skipping for Duchenne Muscular Dystrophy
  • Systemic Treatment of Duchenne Muscular Dystrophy by Antisense Oligomer-Induced Exon Skipping
  • RNAi Therapy for Dominant Muscular Dystrophies and Other Myopathies
  • Combinatorial Gene Therapy Strategies for Treating Muscular Dystrophies
  • Duchenne Cardiomyopathy Gene Therapy
  • Systemic Gene Delivery for Muscle Gene Therapy
  • Modulating Immune Responses in Muscle Gene Therapy
  • Delivering Large Therapeutic Genes for Muscle Gene Therapy
  • Muscle as a Metabolic Factory for Gene Therapy
  • Muscle as a Target for Genetic Vaccine
  • Combining Stem Cells and Exon Skipping Strategy to Treat Muscular Dystrophy
  • Gene Therapy Clinical Trials for Muscular Dystrophies.