Stem Cell Therapy in Lysosomal Storage Diseases

• Συγγραφή απο Οργανισμό/Αρχή: SpringerLink (Online service)
• Άλλοι συγγραφείς: Boelens, Jaap Jan (Επιμελητής έκδοσης), Wynn, Robert (Επιμελητής έκδοσης)
• Μορφή: Ηλεκτρονική πηγή Ηλ. βιβλίο
• Γλώσσα: English
• Έκδοση: New York, NY : Springer New York : Imprint: Humana Press, 2013.
• Σειρά: Stem Cell Biology and Regenerative Medicine,
• Θέματα: Life sciences.; Human genetics.; Cell biology.; Stem cells.; Life Sciences.; Stem Cells.; Cell Biology.; Human Genetics.
• Φυσική περιγραφή: IX, 171 p. 6 illus., 3 illus. in color. online resource.
• ISBN: 9781461483571
• ISSN: 2196-8985

Stem Cell therapy for lysosomal diseases (LSDs) is developing rapidly. This volume discusses the history, current practice and future perspectives of stem cells in inborn errors of metabolism (IEM) and provides an international perspective on progress, limitations, and future directions (e.g. gene therapy, iPS, ES) in the field. Beginning with an overview of these diseases, the book covers the breadth of this topic from treatment options, bone marrow transplantation, and alternative treatment options, through long-term outcomes and future perspectives.