Stem Cell Therapy in Lysosomal Storage Diseases

Stem Cell therapy for lysosomal diseases (LSDs) is developing rapidly. This volume discusses the history, current practice and future perspectives of stem cells in inborn errors of metabolism (IEM) and provides an international perspective on progress, limitations, and future directions (e.g. gene t...

Πλήρης περιγραφή

Λεπτομέρειες βιβλιογραφικής εγγραφής
Συγγραφή απο Οργανισμό/Αρχή: SpringerLink (Online service)
Άλλοι συγγραφείς: Boelens, Jaap Jan (Επιμελητής έκδοσης), Wynn, Robert (Επιμελητής έκδοσης)
Μορφή: Ηλεκτρονική πηγή Ηλ. βιβλίο
Γλώσσα:English
Έκδοση: New York, NY : Springer New York : Imprint: Humana Press, 2013.
Σειρά:Stem Cell Biology and Regenerative Medicine,
Θέματα:
Διαθέσιμο Online:Full Text via HEAL-Link
LEADER 02895nam a22005055i 4500
001 978-1-4614-8357-1
003 DE-He213
005 20151030081222.0
007 cr nn 008mamaa
008 131010s2013 xxu| s |||| 0|eng d
020 |a 9781461483571  |9 978-1-4614-8357-1 
024 7 |a 10.1007/978-1-4614-8357-1  |2 doi 
040 |d GrThAP 
050 4 |a QH588.S83 
072 7 |a PSAK  |2 bicssc 
072 7 |a SCI017000  |2 bisacsh 
072 7 |a SCI049000  |2 bisacsh 
082 0 4 |a 571.6  |2 23 
245 1 0 |a Stem Cell Therapy in Lysosomal Storage Diseases  |h [electronic resource] /  |c edited by Jaap Jan Boelens, Robert Wynn. 
264 1 |a New York, NY :  |b Springer New York :  |b Imprint: Humana Press,  |c 2013. 
300 |a IX, 171 p. 6 illus., 3 illus. in color.  |b online resource. 
336 |a text  |b txt  |2 rdacontent 
337 |a computer  |b c  |2 rdamedia 
338 |a online resource  |b cr  |2 rdacarrier 
347 |a text file  |b PDF  |2 rda 
490 1 |a Stem Cell Biology and Regenerative Medicine,  |x 2196-8985 
505 0 |a 1. Lysosomal Diseases and Therapeutic Options: An Overview -- 2. Alternative Treatment Options: Enzyme Replacement and Small Molecule Therapies -- 3. Hematopoietic Cell Transplantation in Inborn Errors of Metabolism -- 4. Allogeneic Hematopoietic Stem Cell Transplantation in Lysosomal Storage Disorders: Long Term Neurodevelopmental and Somatic Outcome -- 5. Hematopoietic Stem Cell Gene Therapy for Lysosomal Storage Disorders: Expected Benefits and Limitations -- 6. Alternative Future Therapies for Lysosomal Storage Diseases: Embryonic Stem Cell- and Induced Pluripotent Stem Cell Therapy -- 7. New Directions and Conclusions. 
520 |a Stem Cell therapy for lysosomal diseases (LSDs) is developing rapidly. This volume discusses the history, current practice and future perspectives of stem cells in inborn errors of metabolism (IEM) and provides an international perspective on progress, limitations, and future directions (e.g. gene therapy, iPS, ES) in the field. Beginning with an overview of these diseases, the book covers the breadth of this topic from treatment options, bone marrow transplantation, and alternative treatment options, through long-term outcomes and future perspectives. 
650 0 |a Life sciences. 
650 0 |a Human genetics. 
650 0 |a Cell biology. 
650 0 |a Stem cells. 
650 1 4 |a Life Sciences. 
650 2 4 |a Stem Cells. 
650 2 4 |a Cell Biology. 
650 2 4 |a Human Genetics. 
700 1 |a Boelens, Jaap Jan.  |e editor. 
700 1 |a Wynn, Robert.  |e editor. 
710 2 |a SpringerLink (Online service) 
773 0 |t Springer eBooks 
776 0 8 |i Printed edition:  |z 9781461483564 
830 0 |a Stem Cell Biology and Regenerative Medicine,  |x 2196-8985 
856 4 0 |u http://dx.doi.org/10.1007/978-1-4614-8357-1  |z Full Text via HEAL-Link 
912 |a ZDB-2-SBL 
950 |a Biomedical and Life Sciences (Springer-11642)