Safety and Efficacy of Gene-Based Therapeutics for Inherited Disorders

• Corporate Author: SpringerLink (Online service)
• Other Authors: Brunetti-Pierri, Nicola (Editor)
• Format: Electronic eBook
• Language: English
• Published: Cham : Springer International Publishing : Imprint: Springer, 2017.
• Subjects: Medicine.; Gene therapy.; Molecular biology.; Pharmacology.; Biomedicine.; Pharmacology/Toxicology.; Gene Therapy.; Molecular Medicine.

In this book, leading international experts analyze state-of-the-art advances in gene transfer vectors for applications in inherited disorders and also examine the toxicity profiles of these methods. The authors discuss the strengths and weaknesses of available vectors in the clinical setting, and s...